Dyne Therapeutics Shares Rise After Announcing Positive Topline Results for z-rostudirsen in Phase 1/2 DMD Trial

The DELIVER proceedings besides provided caller affirmative semipermanent objective information from its ongoing open-label hold and semipermanent hold portions. Z-rostudirsen is an investigational therapeutic utilizing Dyne’s FORCE platform, designed to alteration the accumulation of adjacent full-length dystrophin by conjugating a phosphorodiamidate morpholino oligomer to an antigen-binding fragment that binds to the transferrin receptor 1.

The cause has received Breakthrough Therapy, Fast Track, and Rare Pediatric Disease designations from the US FDA, arsenic good arsenic Orphan Drug designation from the FDA, EMA, and MHLW successful Japan. The REC met its superior endpoint and showed a statistically important summation successful musculus content-adjusted dystrophin look to 5.46% of mean comparative to baseline astatine 6 months. Functional betterment was observed crossed each 6 prespecified objective endpoints astatine 6 months comparative to baseline and declines successful the pooled placebo group. Dyne is connected way to taxable a Biologics License Application/BLA for US Accelerated Approval successful Q2 2026.

Dyne Therapeutics Inc. (NASDAQ:DYN) is simply a clinical-stage neuromuscular illness institution that discovers and develops therapeutics for neuromuscular diseases successful the US.

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